corpus.blog
43,134 blogs · 5,445,103 posts Claim your blog
Record · corpus.blog/posts/01a0879b-f8c4-7375-8fc9-75ea6e23533e

Notable Recent Events in Gene Therapy Translation January 2023 to January 2026

logancollinsblog.com · published 4 February 2026

A record is what was published and who pointed at it. The text of the post is not held here: read it at the source, or at its Wayback capture.

Read the post at logancollinsblog.com Wayback capture
0blogs citing
First cited
—
Most recent
—
Rank this month
not ranked
External links
43
Words captured
3,172

Cited by

No blog we hold has cited this post yet.

Links from this post

Link
Host
https://www.fda.gov/news-events/press-announcements/fda-approves-first-gene-therapy-adults-severe-hemophilia
fda.gov
https://www.fda.gov/news-events/press-announcements/fda-approves-first-gene-therapy-treatment-certain-patients-duchenne-muscular-dystrophy
fda.gov
https://www.fiercepharma.com/pharma/sareptas-dmd-gene-therapy-finally-makes-it-accelerated-approval-finish-line-restricted
fiercepharma.com
https://investorrelations.sarepta.com/news-releases/news-release-details/sarepta-therapeutics-announces-topline-results-embark-global-0
investorrelations.sarepta.com
https://www.biospace.com/sarepta-fails-confirmatory-trial-for-dmd-therapy-still-eyes-label-expansion
biospace.com
https://www.parentprojectmd.org/fda-accepts-efficacy-supplement-to-expand-elevidys-indication/
parentprojectmd.org
https://www.sarepta.com/community-letter-elevidys-safety-update
sarepta.com
https://www.reuters.com/business/healthcare-pharmaceuticals/fda-investigates-patient-deaths-after-treatment-with-sareptas-gene-therapy-2025-06-24/
reuters.com
https://www.fiercepharma.com/pharma/sarepta-getting-back-fdas-good-side-pauses-shipments-duchenne-gene-therapy-elevidys
fiercepharma.com
https://investorrelations.sarepta.com/news-releases/news-release-details/sarepta-therapeutics-announces-pipeline-progress-multiple-limb
investorrelations.sarepta.com
https://www.fda.gov/news-events/press-announcements/fda-requests-sarepta-therapeutics-suspend-distribution-elevidys-and-places-clinical-trials-hold
fda.gov
https://www.reuters.com/sustainability/boards-policy-regulation/roche-pauses-shipments-elevidys-gene-therapy-outside-us-2025-07-22/
reuters.com
https://www.biopharmadive.com/news/sarepta-layoffs-restructuring-elevidys-duchenne-research-cuts/753256/
biopharmadive.com
https://www.roche.com/media/releases/med-cor-2025-07-25
roche.com
https://www.fda.gov/news-events/press-announcements/fda-investigating-death-8-year-old-boy-who-received-elevidys
fda.gov
https://investorrelations.sarepta.com/news-releases/news-release-details/sarepta-therapeutics-provides-clarifying-statement-elevidys
investorrelations.sarepta.com
https://www.fda.gov/news-events/press-announcements/fda-approves-new-safety-warning-and-revised-indication-limits-use-elevidys-following-reports-fatal
fda.gov
https://investors.vrtx.com/news-releases/news-release-details/vertex-and-crispr-therapeutics-announce-authorization-first
investors.vrtx.com
https://www.fda.gov/news-events/press-announcements/fda-approves-first-gene-therapies-treat-patients-sickle-cell-disease
fda.gov
https://investors.vrtx.com/news-releases/news-release-details/vertex-announces-us-fda-approval-casgevytm-exagamglogene
investors.vrtx.com
https://www.fda.gov/news-events/press-announcements/fda-approves-first-gene-therapy-children-metachromatic-leukodystrophy
fda.gov
https://www.fda.gov/news-events/press-announcements/fda-approves-first-topical-gene-therapy-treatment-wounds-patients-dystrophic-epidermolysis-bullosa
fda.gov
https://www.fda.gov/vaccines-blood-biologics/zevaskyn
fda.gov
https://www.nature.com/articles/d41573-025-00082-2
nature.com
https://www.pfizer.com/news/press-release/press-release-detail/us-fda-approves-pfizers-beqveztm-fidanacogene-elaparvovec
pfizer.com
https://www.cgtlive.com/view/pfizer-jettisons-fda-approved-hemophilia-b-gene-therapy-beqvez
cgtlive.com
https://www.cgtlive.com/view/patient-dies-after-treatment-rocket-pharmaceuticals-danon-disease-gene-therapy-rp-a501-phase-2-trial
cgtlive.com
https://ir.rocketpharma.com/news-releases/news-release-details/rocket-pharmaceuticals-announces-fda-has-lifted-clinical-hold
ir.rocketpharma.com
https://ir.intelliatx.com/news-releases/news-release-details/intellia-announces-positive-clinical-proof-concept-data-redosing
ir.intelliatx.com
https://www.cgtlive.com/view/intellia-phase-3-trials-transthyretin-amyloidosis-gene-editing-therapy-nex-z-hold-grade-4-liver-ae
cgtlive.com
https://ir.intelliatx.com/news-releases/news-release-details/intellia-therapeutics-announces-fda-lift-clinical-hold-magnitude
ir.intelliatx.com
https://uniqure.gcs-web.com/news-releases/news-release-details/uniqure-announces-alignment-fda-key-elements-accelerated
uniqure.gcs-web.com
https://www.uniqure.com/programs-pipeline/huntingtons-disease
uniqure.com
https://www.uniqure.com/programs-pipeline/phase-1-2-clinical-trial-of-amt-130
uniqure.com
https://www.fiercebiotech.com/biotech/uniqure-hopes-launch-1st-huntingtons-gene-therapy-next-year-following-phase-12-success
fiercebiotech.com
https://www.fiercebiotech.com/biotech/fierce-biotech-layoff-tracker-2026
fiercebiotech.com
https://www.fiercebiotech.com/biotech/capsida-pauses-phase-1-gene-therapy-trial-after-child-dies
fiercebiotech.com
https://capsida.com/an-important-update-regarding-our-cap-002-program-a-letter-to-the-stxbp1-community/
capsida.com
https://ir.replimune.com/news-releases/news-release-details/replimune-receives-complete-response-letter-fda-rp1-biologics
ir.replimune.com
https://ir.replimune.com/news-releases/news-release-details/replimune-announces-fda-acceptance-bla-resubmission-rp1-0
ir.replimune.com
https://investors.beamtx.com/news-releases/news-release-details/beam-therapeutics-announces-positive-initial-data-beam-302-phase
investors.beamtx.com
https://investors.beamtx.com/news-releases/news-release-details/beam-therapeutics-announces-clearance-investigational-new-drug
investors.beamtx.com
https://investors.beamtx.com/news-releases/news-release-details/beam-therapeutics-reports-updated-data-beacon-phase-12-trial
investors.beamtx.com
Elsewhere on logancollinsblog.com (1)