41554 blogs · [ { "id": "01a08765-9cab-73b6-aa2d-529ea2aa4dfe", "title": "Our public comment on FDA's Expedited IND Pilot Program", "url": "http://www.cureffi.org/2026/09/02/public-comment-expedited-ind/", "published_at": "2026-09-02T00:00:00+00:00" }, { "id": "01a08765-9cab-73b6-aa2d-529ea2f9fd1b", "title": "Jeff Carroll: searching for the toxic species in Huntington's disease", "url": "http://www.cureffi.org/2026/08/10/jeff-carroll-seminar/", "published_at": "2026-08-10T00:00:00+00:00" }, { "id": "01a08765-9cab-73b6-aa2d-529ea3981e71", "title": "Robert Thorne: blood-brain barrier primer", "url": "http://www.cureffi.org/2026/07/13/bbb-primer/", "published_at": "2026-07-13T00:00:00+00:00" }, { "id": "01a08765-9cab-73b6-aa2d-529ea4345adf", "title": "Why TAPCJD is so important", "url": "http://www.cureffi.org/2026/06/02/why-tapcjd-is-so-important/", "published_at": "2026-06-02T00:00:00+00:00" }, { "id": "01a08765-9cab-73b6-aa2d-529ea4cc9190", "title": "Divalent siRNA clinical trial is now recruiting", "url": "http://www.cureffi.org/2026/04/22/divalent-sirna-clinical-trial-is-now-recruiting/", "published_at": "2026-04-22T00:00:00+00:00" }, { "id": "01a08765-9cab-73b6-aa2d-529ea5726673", "title": "ION717 trial re-opens with 3rd dosing regimen", "url": "http://www.cureffi.org/2026/03/17/ion717-trial-reopens/", "published_at": "2026-03-17T00:00:00+00:00" }, { "id": "01a08765-9cab-73b6-aa2d-529ea57e8b27", "title": "Celebrating Byron Caughey, 1957-2026", "url": "http://www.cureffi.org/2026/02/18/celebrating-byron-caughey/", "published_at": "2026-02-18T00:00:00+00:00" }, { "id": "01a08765-9cab-73b6-aa2d-529ea58772a8", "title": "Uniqure reports that AMT-130 slows Huntington's disease", "url": "http://www.cureffi.org/2025/10/08/amt-130/", "published_at": "2025-10-08T00:00:00+00:00" }, { "id": "01a08765-9cab-73b6-aa2d-529ea59a77c1", "title": "Evidence that the effect of C-terminal truncating variants in PRNP may be position-dependent", "url": "http://www.cureffi.org/2025/07/04/evidence-truncating-position-dependent/", "published_at": "2025-07-04T00:00:00+00:00" }, { "id": "01a08765-9cab-73b6-aa2d-529ea5df028b", "title": "We have an open IND. What comes next?", "url": "http://www.cureffi.org/2025/04/14/open-ind-whats-next/", "published_at": "2025-04-14T00:00:00+00:00" } ] posts Claim your blog
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